Pioneering Gene Therapy for Rare Genetic Disorders

{
  "id": "10.2128/pr.12992",
  "pubType": "Proposal",
  "published": false,
  "title": "Pioneering Gene Therapy for Rare Genetic Disorders",
  "content": "This proposal focuses on developing gene therapies for rare genetic disorders, potentially providing life-saving treatments to patients with limited options.",
  "budget": "$12,000,000",
  "objectives": [
    "Identify and target specific genetic mutations",
    "Conduct clinical trials to test therapy efficacy and safety"
  ],
  "challenges": [
    "Ethical concerns and regulatory approval",
    "Scaling up production for widespread clinical use"
  ]
}